Recombinant Adeno-Associated Virus-Mediated In Utero Gene Transfer Gives Therapeutic Transgene Expression in the Sheep
Somatic in utero gene therapy aims to treat congenital diseases where pathology develops in perinatal life, thereby preventing permanent damage. The aim of this study was to determine whether delivery of self-complementary (sc) adeno-associated virus (AAV) vector in utero would provide therapeutic l...
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| Main Author: | Abi Nader, Khalil (author) |
|---|---|
| Other Authors: | David, Anna L. (author), McIntosh, Jenny (author), Peebles, Donald (author), Cook, Terry (author), Waddington, Simon (author), Weisz, Boaz (author) |
| Format: | article |
| Published: |
2011
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| Online Access: | http://hdl.handle.net/10725/3970 http://dx.doi.org/10.1089/hum.2010.007. http://libraries.lau.edu.lb/research/laur/terms-of-use/articles.php http://online.liebertpub.com/doi/abs/10.1089/hum.2010.007 |
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