Recombinant Adeno-Associated Virus-Mediated In Utero Gene Transfer Gives Therapeutic Transgene Expression in the Sheep

Recombinant Adeno-Associated Virus-Mediated In Utero Gene Transfer Gives Therapeutic Transgene Expression in the Sheep

Somatic in utero gene therapy aims to treat congenital diseases where pathology develops in perinatal life, thereby preventing permanent damage. The aim of this study was to determine whether delivery of self-complementary (sc) adeno-associated virus (AAV) vector in utero would provide therapeutic l...

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Bibliographic Details
Main Author: Abi Nader, Khalil (author)
Other Authors: David, Anna L. (author), McIntosh, Jenny (author), Peebles, Donald (author), Cook, Terry (author), Waddington, Simon (author), Weisz, Boaz (author)
Format: article
Published: 2011
Online Access:http://hdl.handle.net/10725/3970
http://dx.doi.org/10.1089/hum.2010.007.
http://libraries.lau.edu.lb/research/laur/terms-of-use/articles.php
http://online.liebertpub.com/doi/abs/10.1089/hum.2010.007
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http://hdl.handle.net/10725/3970
http://dx.doi.org/10.1089/hum.2010.007.
http://libraries.lau.edu.lb/research/laur/terms-of-use/articles.php
http://online.liebertpub.com/doi/abs/10.1089/hum.2010.007

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