An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety

<p>This review synthesizes the current evidence to assess the efficacy and safety of caplacizumab in the treatment of iTTP, focusing on its impact on TPE requirements, time to platelet normalization, relapse prevention, and treatment-related adverse events. Thirteen studies (11 observational a...

وصف كامل

محفوظ في:
التفاصيل البيبلوغرافية
المؤلف الرئيسي: Mohamed Yassin (4166515) (author)
مؤلفون آخرون: Rola Ghasoub (16555851) (author), Neda Jafari (22963048) (author), Lulwah Al-Tourah (22963051) (author), Anas Babiker (22963054) (author), Muna AlRasheed (22963057) (author)
منشور في: 2025
الموضوعات:
الوسوم: إضافة وسم
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author Mohamed Yassin (4166515)
author2 Rola Ghasoub (16555851)
Neda Jafari (22963048)
Lulwah Al-Tourah (22963051)
Anas Babiker (22963054)
Muna AlRasheed (22963057)
author2_role author
author
author
author
author
author_facet Mohamed Yassin (4166515)
Rola Ghasoub (16555851)
Neda Jafari (22963048)
Lulwah Al-Tourah (22963051)
Anas Babiker (22963054)
Muna AlRasheed (22963057)
author_role author
dc.creator.none.fl_str_mv Mohamed Yassin (4166515)
Rola Ghasoub (16555851)
Neda Jafari (22963048)
Lulwah Al-Tourah (22963051)
Anas Babiker (22963054)
Muna AlRasheed (22963057)
dc.date.none.fl_str_mv 2025-12-20T09:00:00Z
dc.identifier.none.fl_str_mv 10.1016/j.blre.2025.101359
dc.relation.none.fl_str_mv https://figshare.com/articles/journal_contribution/An_updated_systematic_review_and_meta-analysis_of_Caplacizumab_for_immune_thrombotic_thrombocytopenic_purpura_Insights_into_efficacy_and_safety/31017343
dc.rights.none.fl_str_mv CC BY 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biomedical and clinical sciences
Cardiovascular medicine and haematology
Pharmacology and pharmaceutical sciences
Caplacizumab
Immune thrombotic thrombocytopenic purpura
Thrombotic thrombocytopenic purpura
Therapeutic plasma exchange
iTTP
dc.title.none.fl_str_mv An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
dc.type.none.fl_str_mv Text
Journal contribution
info:eu-repo/semantics/publishedVersion
text
contribution to journal
description <p>This review synthesizes the current evidence to assess the efficacy and safety of caplacizumab in the treatment of iTTP, focusing on its impact on TPE requirements, time to platelet normalization, relapse prevention, and treatment-related adverse events. Thirteen studies (11 observational and 2 RCTs), involving 2956 patients with iTTP were included. The majority of included studies were of high methodological quality, indicating a low risk of bias based on the assessment tools. The analysis found that caplacizumab was associated with significant clinical benefits. It marked a reduction in daily TPE sessions (MD = −3.92, p < 0.001) and time to platelet normalization (MD = −2.44, p = 0.03). Caplacizumab also significantly reduced mortality (RR = 0.29, p < 0.001) and iTTP exacerbations (RR = 0.27, p < 0.001), leading to shorter hospital stays (MD = −5.13, p = 0.001). Caplacizumab demonstrated notable clinical benefits in managing iTTP, with significant reductions in daily TPE sessions, time to platelet normalization, mortality, and iTTP exacerbations. Promising results were also noticed for early initiation compared to delayed initiation.</p><h2>Other Information</h2> <p> Published in: Blood Reviews<br> License: <a href="http://creativecommons.org/licenses/by/4.0/" target="_blank">http://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1016/j.blre.2025.101359" target="_blank">https://dx.doi.org/10.1016/j.blre.2025.101359</a></p>
eu_rights_str_mv openAccess
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identifier_str_mv 10.1016/j.blre.2025.101359
network_acronym_str Manara2
network_name_str Manara2
oai_identifier_str oai:figshare.com:article/31017343
publishDate 2025
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spelling An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safetyMohamed Yassin (4166515)Rola Ghasoub (16555851)Neda Jafari (22963048)Lulwah Al-Tourah (22963051)Anas Babiker (22963054)Muna AlRasheed (22963057)Biomedical and clinical sciencesCardiovascular medicine and haematologyPharmacology and pharmaceutical sciencesCaplacizumabImmune thrombotic thrombocytopenic purpuraThrombotic thrombocytopenic purpuraTherapeutic plasma exchangeiTTP<p>This review synthesizes the current evidence to assess the efficacy and safety of caplacizumab in the treatment of iTTP, focusing on its impact on TPE requirements, time to platelet normalization, relapse prevention, and treatment-related adverse events. Thirteen studies (11 observational and 2 RCTs), involving 2956 patients with iTTP were included. The majority of included studies were of high methodological quality, indicating a low risk of bias based on the assessment tools. The analysis found that caplacizumab was associated with significant clinical benefits. It marked a reduction in daily TPE sessions (MD = −3.92, p < 0.001) and time to platelet normalization (MD = −2.44, p = 0.03). Caplacizumab also significantly reduced mortality (RR = 0.29, p < 0.001) and iTTP exacerbations (RR = 0.27, p < 0.001), leading to shorter hospital stays (MD = −5.13, p = 0.001). Caplacizumab demonstrated notable clinical benefits in managing iTTP, with significant reductions in daily TPE sessions, time to platelet normalization, mortality, and iTTP exacerbations. Promising results were also noticed for early initiation compared to delayed initiation.</p><h2>Other Information</h2> <p> Published in: Blood Reviews<br> License: <a href="http://creativecommons.org/licenses/by/4.0/" target="_blank">http://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1016/j.blre.2025.101359" target="_blank">https://dx.doi.org/10.1016/j.blre.2025.101359</a></p>2025-12-20T09:00:00ZTextJournal contributioninfo:eu-repo/semantics/publishedVersiontextcontribution to journal10.1016/j.blre.2025.101359https://figshare.com/articles/journal_contribution/An_updated_systematic_review_and_meta-analysis_of_Caplacizumab_for_immune_thrombotic_thrombocytopenic_purpura_Insights_into_efficacy_and_safety/31017343CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/310173432025-12-20T09:00:00Z
spellingShingle An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
Mohamed Yassin (4166515)
Biomedical and clinical sciences
Cardiovascular medicine and haematology
Pharmacology and pharmaceutical sciences
Caplacizumab
Immune thrombotic thrombocytopenic purpura
Thrombotic thrombocytopenic purpura
Therapeutic plasma exchange
iTTP
status_str publishedVersion
title An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
title_full An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
title_fullStr An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
title_full_unstemmed An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
title_short An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
title_sort An updated systematic review and meta-analysis of Caplacizumab for immune thrombotic thrombocytopenic purpura: Insights into efficacy and safety
topic Biomedical and clinical sciences
Cardiovascular medicine and haematology
Pharmacology and pharmaceutical sciences
Caplacizumab
Immune thrombotic thrombocytopenic purpura
Thrombotic thrombocytopenic purpura
Therapeutic plasma exchange
iTTP