Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria

<p>Homocystinuria (HCU) is a rare autosomal recessive inherited disorder usually diagnosed in childhood. It is characterized by a deficiency of the enzyme that converts homocysteine to cystathionine. The accumulation of homocysteine leads to abnormalities in the ocular, skeletal, cardiovascula...

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محفوظ في:
التفاصيل البيبلوغرافية
المؤلف الرئيسي: Aasir M. Suliman (14150217) (author)
مؤلفون آخرون: Mohamed A. Alamin (17871587) (author), Maha M. Hamza (17871590) (author)
منشور في: 2023
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author Aasir M. Suliman (14150217)
author2 Mohamed A. Alamin (17871587)
Maha M. Hamza (17871590)
author2_role author
author
author_facet Aasir M. Suliman (14150217)
Mohamed A. Alamin (17871587)
Maha M. Hamza (17871590)
author_role author
dc.creator.none.fl_str_mv Aasir M. Suliman (14150217)
Mohamed A. Alamin (17871587)
Maha M. Hamza (17871590)
dc.date.none.fl_str_mv 2023-01-01T00:00:00Z
dc.identifier.none.fl_str_mv 10.1016/j.rmcr.2023.101808
dc.relation.none.fl_str_mv https://figshare.com/articles/journal_contribution/Tracheobronchomegaly_Mounier-Kuhn_syndrome_and_Bronchiectasis_as_rare_manifestations_of_Homocystinuria/25109444
dc.rights.none.fl_str_mv CC BY 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biomedical and clinical sciences
Cardiovascular medicine and haematology
Homocystinuria
Bronchiectasis
Tracheobronchomegaly
Mounier-Kuhn syndrome
Fibrillin degeneration
dc.title.none.fl_str_mv Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
dc.type.none.fl_str_mv Text
Journal contribution
info:eu-repo/semantics/publishedVersion
text
contribution to journal
description <p>Homocystinuria (HCU) is a rare autosomal recessive inherited disorder usually diagnosed in childhood. It is characterized by a deficiency of the enzyme that converts homocysteine to cystathionine. The accumulation of homocysteine leads to abnormalities in the ocular, skeletal, cardiovascular, and central nervous systems. HCU shares several clinical features with Marfan syndrome; however, respiratory system involvement in HCU is uncommon and rarely reported. Bronchiectasis has been previously reported in a few cases of HCU, and it was attributed mainly to fibrillin deficiency. This case describes a young girl diagnosed with classical HCU since childhood who presented with a chronic productive cough and was initially misdiagnosed as bronchial Asthma. However, upon further evaluation, she was eventually diagnosed with tracheobronchomegaly (TBM), or Mounier-Kuhn Syndrome, and bronchiectasis based on the computed tomography (CT) scan of chest findings. To our knowledge, this is the first reported case of TBM and bronchiectasis in HCU. We believe that fibrillin degeneration may be the key to understanding this unusual association in HCU.</p><h2>Other Information</h2> <p> Published in: Respiratory Medicine Case Reports<br> License: <a href="http://creativecommons.org/licenses/by/4.0/" target="_blank">http://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1016/j.rmcr.2023.101808" target="_blank">https://dx.doi.org/10.1016/j.rmcr.2023.101808</a></p>
eu_rights_str_mv openAccess
id Manara2_693c64d1df3d24d84b34424f587f66a6
identifier_str_mv 10.1016/j.rmcr.2023.101808
network_acronym_str Manara2
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oai_identifier_str oai:figshare.com:article/25109444
publishDate 2023
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spelling Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of HomocystinuriaAasir M. Suliman (14150217)Mohamed A. Alamin (17871587)Maha M. Hamza (17871590)Biomedical and clinical sciencesCardiovascular medicine and haematologyHomocystinuriaBronchiectasisTracheobronchomegalyMounier-Kuhn syndromeFibrillin degeneration<p>Homocystinuria (HCU) is a rare autosomal recessive inherited disorder usually diagnosed in childhood. It is characterized by a deficiency of the enzyme that converts homocysteine to cystathionine. The accumulation of homocysteine leads to abnormalities in the ocular, skeletal, cardiovascular, and central nervous systems. HCU shares several clinical features with Marfan syndrome; however, respiratory system involvement in HCU is uncommon and rarely reported. Bronchiectasis has been previously reported in a few cases of HCU, and it was attributed mainly to fibrillin deficiency. This case describes a young girl diagnosed with classical HCU since childhood who presented with a chronic productive cough and was initially misdiagnosed as bronchial Asthma. However, upon further evaluation, she was eventually diagnosed with tracheobronchomegaly (TBM), or Mounier-Kuhn Syndrome, and bronchiectasis based on the computed tomography (CT) scan of chest findings. To our knowledge, this is the first reported case of TBM and bronchiectasis in HCU. We believe that fibrillin degeneration may be the key to understanding this unusual association in HCU.</p><h2>Other Information</h2> <p> Published in: Respiratory Medicine Case Reports<br> License: <a href="http://creativecommons.org/licenses/by/4.0/" target="_blank">http://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1016/j.rmcr.2023.101808" target="_blank">https://dx.doi.org/10.1016/j.rmcr.2023.101808</a></p>2023-01-01T00:00:00ZTextJournal contributioninfo:eu-repo/semantics/publishedVersiontextcontribution to journal10.1016/j.rmcr.2023.101808https://figshare.com/articles/journal_contribution/Tracheobronchomegaly_Mounier-Kuhn_syndrome_and_Bronchiectasis_as_rare_manifestations_of_Homocystinuria/25109444CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/251094442023-01-01T00:00:00Z
spellingShingle Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
Aasir M. Suliman (14150217)
Biomedical and clinical sciences
Cardiovascular medicine and haematology
Homocystinuria
Bronchiectasis
Tracheobronchomegaly
Mounier-Kuhn syndrome
Fibrillin degeneration
status_str publishedVersion
title Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
title_full Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
title_fullStr Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
title_full_unstemmed Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
title_short Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
title_sort Tracheobronchomegaly (Mounier-Kuhn syndrome) and Bronchiectasis as rare manifestations of Homocystinuria
topic Biomedical and clinical sciences
Cardiovascular medicine and haematology
Homocystinuria
Bronchiectasis
Tracheobronchomegaly
Mounier-Kuhn syndrome
Fibrillin degeneration