Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank

<h3>Background</h3><p dir="ltr">The genetic architecture underlying Familial Hypercholesterolemia (FH) in Middle Eastern Arabs is yet to be fully described, and approaches to assess this from population-wide biobanks are important for public health planning and personaliz...

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Main Author: Geethanjali Devadoss Gandhi (14056966) (author)
Other Authors: Waleed Aamer (14056969) (author), Navaneethakrishnan Krishnamoorthy (391608) (author), Najeeb Syed (12561967) (author), Elbay Aliyev (14056972) (author), Aljazi Al-Maraghi (14056975) (author), Muhammad Kohailan (748774) (author), Jamil Alenbawi (14056978) (author), Mohammed Elanbari (11822375) (author), Borbala Mifsud (3907267) (author), Younes Mokrab (6367) (author), Charbel Abi Khalil (781797) (author), Khalid A. Fakhro (3158862) (author), Qatar Genome Program Research Consortium (QGPRC) (18295378) (author)
Published: 2022
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_version_ 1864513516854050816
author Geethanjali Devadoss Gandhi (14056966)
author2 Waleed Aamer (14056969)
Navaneethakrishnan Krishnamoorthy (391608)
Najeeb Syed (12561967)
Elbay Aliyev (14056972)
Aljazi Al-Maraghi (14056975)
Muhammad Kohailan (748774)
Jamil Alenbawi (14056978)
Mohammed Elanbari (11822375)
Borbala Mifsud (3907267)
Younes Mokrab (6367)
Charbel Abi Khalil (781797)
Khalid A. Fakhro (3158862)
Qatar Genome Program Research Consortium (QGPRC) (18295378)
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author_facet Geethanjali Devadoss Gandhi (14056966)
Waleed Aamer (14056969)
Navaneethakrishnan Krishnamoorthy (391608)
Najeeb Syed (12561967)
Elbay Aliyev (14056972)
Aljazi Al-Maraghi (14056975)
Muhammad Kohailan (748774)
Jamil Alenbawi (14056978)
Mohammed Elanbari (11822375)
Borbala Mifsud (3907267)
Younes Mokrab (6367)
Charbel Abi Khalil (781797)
Khalid A. Fakhro (3158862)
Qatar Genome Program Research Consortium (QGPRC) (18295378)
author_role author
dc.creator.none.fl_str_mv Geethanjali Devadoss Gandhi (14056966)
Waleed Aamer (14056969)
Navaneethakrishnan Krishnamoorthy (391608)
Najeeb Syed (12561967)
Elbay Aliyev (14056972)
Aljazi Al-Maraghi (14056975)
Muhammad Kohailan (748774)
Jamil Alenbawi (14056978)
Mohammed Elanbari (11822375)
Borbala Mifsud (3907267)
Younes Mokrab (6367)
Charbel Abi Khalil (781797)
Khalid A. Fakhro (3158862)
Qatar Genome Program Research Consortium (QGPRC) (18295378)
dc.date.none.fl_str_mv 2022-11-03T03:00:00Z
dc.identifier.none.fl_str_mv 10.1186/s12967-022-03697-w
dc.relation.none.fl_str_mv https://figshare.com/articles/journal_contribution/Assessing_the_genetic_burden_of_familial_hypercholesterolemia_in_a_large_middle_eastern_biobank/25532941
dc.rights.none.fl_str_mv CC BY 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biological sciences
Biochemistry and cell biology
Genetics
Biomedical and clinical sciences
Clinical sciences
Cholesterol
Dyslipidemias
LDL
Lipoproteins/Receptors
Premature coronary artery disease
Dutch lipid Clinic Network
LDLRAP1
Sitosterolemia
Polygenic risk scores
Middle East region
dc.title.none.fl_str_mv Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
dc.type.none.fl_str_mv Text
Journal contribution
info:eu-repo/semantics/publishedVersion
text
contribution to journal
description <h3>Background</h3><p dir="ltr">The genetic architecture underlying Familial Hypercholesterolemia (FH) in Middle Eastern Arabs is yet to be fully described, and approaches to assess this from population-wide biobanks are important for public health planning and personalized medicine.</p><h3>Methods</h3><p dir="ltr">We evaluate the pilot phase cohort (n = 6,140 adults) of the Qatar Biobank (QBB) for FH using the Dutch Lipid Clinic Network (DLCN) criteria, followed by an in-depth characterization of all genetic alleles in known dominant (LDLR,APOB, andPCSK9) and recessive (LDLRAP1,ABCG5,ABCG8, andLIPA) FH-causing genes derived from whole-genome sequencing (WGS). We also investigate the utility of a globally established 12-SNP polygenic risk score to predict FH individuals in this cohort with Arab ancestry.</p><h3>Results</h3><p dir="ltr">Using DLCN criteria, we identify eight (0.1%) ‘definite’, 41 (0.7%) ‘probable’ and 334 (5.4%) ‘possible’ FH individuals, estimating a prevalence of ‘definite or probable’ FH in the Qatari cohort of ~ 1:125. We identify ten previously known pathogenic single-nucleotide variants (SNVs) and 14 putatively novel SNVs, as well as one novel copy number variant inPCSK9. Further, despite the modest sample size, we identify one homozygote for a known pathogenic variant (ABCG8, p. Gly574Arg, global MAF = 4.49E-05) associated with Sitosterolemia 2. Finally, calculation of polygenic risk scores found that individuals with ‘definite or probable’ FH have a significantly higher LDL-C SNP score than ‘unlikely’ individuals (p = 0.0003), demonstrating its utility in Arab populations.</p><h3>Conclusion</h3><p dir="ltr">We design and implement a standardized approach to phenotyping a population biobank for FH risk followed by systematically identifying known variants and assessing putative novel variants contributing to FH burden in Qatar. Our results motivate similar studies in population-level biobanks – especially those with globally under-represented ancestries – and highlight the importance of genetic screening programs for early detection and management of individuals with high FH risk in health systems.</p><h2>Other Information</h2><p dir="ltr">Published in: Journal of Translational Medicine<br>License: <a href="https://creativecommons.org/licenses/by/4.0" target="_blank">https://creativecommons.org/licenses/by/4.0</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1186/s12967-022-03697-w" target="_blank">https://dx.doi.org/10.1186/s12967-022-03697-w</a></p>
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identifier_str_mv 10.1186/s12967-022-03697-w
network_acronym_str Manara2
network_name_str Manara2
oai_identifier_str oai:figshare.com:article/25532941
publishDate 2022
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rights_invalid_str_mv CC BY 4.0
spelling Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobankGeethanjali Devadoss Gandhi (14056966)Waleed Aamer (14056969)Navaneethakrishnan Krishnamoorthy (391608)Najeeb Syed (12561967)Elbay Aliyev (14056972)Aljazi Al-Maraghi (14056975)Muhammad Kohailan (748774)Jamil Alenbawi (14056978)Mohammed Elanbari (11822375)Borbala Mifsud (3907267)Younes Mokrab (6367)Charbel Abi Khalil (781797)Khalid A. Fakhro (3158862)Qatar Genome Program Research Consortium (QGPRC) (18295378)Biological sciencesBiochemistry and cell biologyGeneticsBiomedical and clinical sciencesClinical sciencesCholesterolDyslipidemiasLDLLipoproteins/ReceptorsPremature coronary artery diseaseDutch lipid Clinic NetworkLDLRAP1SitosterolemiaPolygenic risk scoresMiddle East region<h3>Background</h3><p dir="ltr">The genetic architecture underlying Familial Hypercholesterolemia (FH) in Middle Eastern Arabs is yet to be fully described, and approaches to assess this from population-wide biobanks are important for public health planning and personalized medicine.</p><h3>Methods</h3><p dir="ltr">We evaluate the pilot phase cohort (n = 6,140 adults) of the Qatar Biobank (QBB) for FH using the Dutch Lipid Clinic Network (DLCN) criteria, followed by an in-depth characterization of all genetic alleles in known dominant (LDLR,APOB, andPCSK9) and recessive (LDLRAP1,ABCG5,ABCG8, andLIPA) FH-causing genes derived from whole-genome sequencing (WGS). We also investigate the utility of a globally established 12-SNP polygenic risk score to predict FH individuals in this cohort with Arab ancestry.</p><h3>Results</h3><p dir="ltr">Using DLCN criteria, we identify eight (0.1%) ‘definite’, 41 (0.7%) ‘probable’ and 334 (5.4%) ‘possible’ FH individuals, estimating a prevalence of ‘definite or probable’ FH in the Qatari cohort of ~ 1:125. We identify ten previously known pathogenic single-nucleotide variants (SNVs) and 14 putatively novel SNVs, as well as one novel copy number variant inPCSK9. Further, despite the modest sample size, we identify one homozygote for a known pathogenic variant (ABCG8, p. Gly574Arg, global MAF = 4.49E-05) associated with Sitosterolemia 2. Finally, calculation of polygenic risk scores found that individuals with ‘definite or probable’ FH have a significantly higher LDL-C SNP score than ‘unlikely’ individuals (p = 0.0003), demonstrating its utility in Arab populations.</p><h3>Conclusion</h3><p dir="ltr">We design and implement a standardized approach to phenotyping a population biobank for FH risk followed by systematically identifying known variants and assessing putative novel variants contributing to FH burden in Qatar. Our results motivate similar studies in population-level biobanks – especially those with globally under-represented ancestries – and highlight the importance of genetic screening programs for early detection and management of individuals with high FH risk in health systems.</p><h2>Other Information</h2><p dir="ltr">Published in: Journal of Translational Medicine<br>License: <a href="https://creativecommons.org/licenses/by/4.0" target="_blank">https://creativecommons.org/licenses/by/4.0</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1186/s12967-022-03697-w" target="_blank">https://dx.doi.org/10.1186/s12967-022-03697-w</a></p>2022-11-03T03:00:00ZTextJournal contributioninfo:eu-repo/semantics/publishedVersiontextcontribution to journal10.1186/s12967-022-03697-whttps://figshare.com/articles/journal_contribution/Assessing_the_genetic_burden_of_familial_hypercholesterolemia_in_a_large_middle_eastern_biobank/25532941CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/255329412022-11-03T03:00:00Z
spellingShingle Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
Geethanjali Devadoss Gandhi (14056966)
Biological sciences
Biochemistry and cell biology
Genetics
Biomedical and clinical sciences
Clinical sciences
Cholesterol
Dyslipidemias
LDL
Lipoproteins/Receptors
Premature coronary artery disease
Dutch lipid Clinic Network
LDLRAP1
Sitosterolemia
Polygenic risk scores
Middle East region
status_str publishedVersion
title Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
title_full Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
title_fullStr Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
title_full_unstemmed Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
title_short Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
title_sort Assessing the genetic burden of familial hypercholesterolemia in a large middle eastern biobank
topic Biological sciences
Biochemistry and cell biology
Genetics
Biomedical and clinical sciences
Clinical sciences
Cholesterol
Dyslipidemias
LDL
Lipoproteins/Receptors
Premature coronary artery disease
Dutch lipid Clinic Network
LDLRAP1
Sitosterolemia
Polygenic risk scores
Middle East region