Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome

<p dir="ltr">Fanconi–Bickel Syndrome (FBS) is a rare disorder of carbohydrate metabolism that is characterized by the accumulation of glycogen mainly in the liver. It is inherited in an autosomal recessive manner due to mutations in the <i>SLC2A2</i> gene. <i>SLC2A2...

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Main Author: Sanaa Sharari (12561952) (author)
Other Authors: Basirudeen Kabeer (18295432) (author), Idris Mohammed (751020) (author), Basma Haris (12040355) (author), Igor Pavlovski (12561964) (author), Iman Hawari (12561958) (author), Ajaz Ahmad Bhat (12561955) (author), Mohammed Toufiq (7251596) (author), Sara Tomei (3441323) (author), Rebecca Mathew (6561392) (author), Najeeb Syed (12561967) (author), Sabah Nisar (12561961) (author), Selma Maacha (501715) (author), Jean-Charles Grivel (284645) (author), Damien Chaussabel (26369) (author), Johan Ericsson (49714) (author), Khalid Hussain (110443) (author)
Published: 2022
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_version_ 1864513506604220416
author Sanaa Sharari (12561952)
author2 Basirudeen Kabeer (18295432)
Idris Mohammed (751020)
Basma Haris (12040355)
Igor Pavlovski (12561964)
Iman Hawari (12561958)
Ajaz Ahmad Bhat (12561955)
Mohammed Toufiq (7251596)
Sara Tomei (3441323)
Rebecca Mathew (6561392)
Najeeb Syed (12561967)
Sabah Nisar (12561961)
Selma Maacha (501715)
Jean-Charles Grivel (284645)
Damien Chaussabel (26369)
Johan Ericsson (49714)
Khalid Hussain (110443)
author2_role author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author
author_facet Sanaa Sharari (12561952)
Basirudeen Kabeer (18295432)
Idris Mohammed (751020)
Basma Haris (12040355)
Igor Pavlovski (12561964)
Iman Hawari (12561958)
Ajaz Ahmad Bhat (12561955)
Mohammed Toufiq (7251596)
Sara Tomei (3441323)
Rebecca Mathew (6561392)
Najeeb Syed (12561967)
Sabah Nisar (12561961)
Selma Maacha (501715)
Jean-Charles Grivel (284645)
Damien Chaussabel (26369)
Johan Ericsson (49714)
Khalid Hussain (110443)
author_role author
dc.creator.none.fl_str_mv Sanaa Sharari (12561952)
Basirudeen Kabeer (18295432)
Idris Mohammed (751020)
Basma Haris (12040355)
Igor Pavlovski (12561964)
Iman Hawari (12561958)
Ajaz Ahmad Bhat (12561955)
Mohammed Toufiq (7251596)
Sara Tomei (3441323)
Rebecca Mathew (6561392)
Najeeb Syed (12561967)
Sabah Nisar (12561961)
Selma Maacha (501715)
Jean-Charles Grivel (284645)
Damien Chaussabel (26369)
Johan Ericsson (49714)
Khalid Hussain (110443)
dc.date.none.fl_str_mv 2022-08-29T09:00:00Z
dc.identifier.none.fl_str_mv 10.3390/biomedicines10092114
dc.relation.none.fl_str_mv https://figshare.com/articles/journal_contribution/Understanding_the_Role_of_GLUT2_in_Dysglycemia_Associated_with_Fanconi_Bickel_Syndrome/26869528
dc.rights.none.fl_str_mv CC BY 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Medical biochemistry and metabolomics
Fanconi–Bickel syndrome (FBS)
dysglycemia
glucose transporter 2 (GLUT2)
PBMCs (peripheral blood mononuclear cells)
miRNAs
dc.title.none.fl_str_mv Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
dc.type.none.fl_str_mv Text
Journal contribution
info:eu-repo/semantics/publishedVersion
text
contribution to journal
description <p dir="ltr">Fanconi–Bickel Syndrome (FBS) is a rare disorder of carbohydrate metabolism that is characterized by the accumulation of glycogen mainly in the liver. It is inherited in an autosomal recessive manner due to mutations in the <i>SLC2A2</i> gene. <i>SLC2A2</i> encodes for the glucose transporter GLUT2 and is expressed in tissues that are involved in glucose homeostasis. The molecular mechanisms of dysglycemia in FBS are still not clearly understood. In this study, we report two cases of FBS with classical phenotypes of FBS associated with dysglycemia. Genomic DNA was extracted and analyzed by whole-genome and Sanger sequencing, and patient PBMCs were used for molecular analysis. One patient had an exonic <i>SLC2A2</i> mutation (c.1093C>T in exon 9, R365X), while the other patient had a novel intronic <i>SLC2A2</i> mutation (c.613-7T>G). Surprisingly, the exonic mutation resulted in the overexpression of dysfunctional GLUT2, resulting in the dysregulated expression of other glucose transporters. The intronic mutation did not affect the coding sequence of GLUT2, its expression, or glucose transport activity. However, it was associated with the expression of miRNAs correlated with type 1 diabetes mellitus, with a particular significant overexpression of hsa-miR-29a-3p implicated in insulin production and secretion. Our findings suggest that <i>SLC2A2</i> mutations cause dysglycemia in FBS either by a direct effect on GLUT2 expression and/or activity or, indirectly, by the dysregulated expression of miRNAs implicated in glucose homeostasis.</p><h2>Other Information</h2><p dir="ltr">Published in: Biomedicines<br>License: <a href="https://creativecommons.org/licenses/by/4.0/" target="_blank">https://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.3390/biomedicines10092114" target="_blank">https://dx.doi.org/10.3390/biomedicines10092114</a></p>
eu_rights_str_mv openAccess
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identifier_str_mv 10.3390/biomedicines10092114
network_acronym_str Manara2
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spelling Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel SyndromeSanaa Sharari (12561952)Basirudeen Kabeer (18295432)Idris Mohammed (751020)Basma Haris (12040355)Igor Pavlovski (12561964)Iman Hawari (12561958)Ajaz Ahmad Bhat (12561955)Mohammed Toufiq (7251596)Sara Tomei (3441323)Rebecca Mathew (6561392)Najeeb Syed (12561967)Sabah Nisar (12561961)Selma Maacha (501715)Jean-Charles Grivel (284645)Damien Chaussabel (26369)Johan Ericsson (49714)Khalid Hussain (110443)Biological sciencesGeneticsBiomedical and clinical sciencesClinical sciencesMedical biochemistry and metabolomicsFanconi–Bickel syndrome (FBS)dysglycemiaglucose transporter 2 (GLUT2)PBMCs (peripheral blood mononuclear cells)miRNAs<p dir="ltr">Fanconi–Bickel Syndrome (FBS) is a rare disorder of carbohydrate metabolism that is characterized by the accumulation of glycogen mainly in the liver. It is inherited in an autosomal recessive manner due to mutations in the <i>SLC2A2</i> gene. <i>SLC2A2</i> encodes for the glucose transporter GLUT2 and is expressed in tissues that are involved in glucose homeostasis. The molecular mechanisms of dysglycemia in FBS are still not clearly understood. In this study, we report two cases of FBS with classical phenotypes of FBS associated with dysglycemia. Genomic DNA was extracted and analyzed by whole-genome and Sanger sequencing, and patient PBMCs were used for molecular analysis. One patient had an exonic <i>SLC2A2</i> mutation (c.1093C>T in exon 9, R365X), while the other patient had a novel intronic <i>SLC2A2</i> mutation (c.613-7T>G). Surprisingly, the exonic mutation resulted in the overexpression of dysfunctional GLUT2, resulting in the dysregulated expression of other glucose transporters. The intronic mutation did not affect the coding sequence of GLUT2, its expression, or glucose transport activity. However, it was associated with the expression of miRNAs correlated with type 1 diabetes mellitus, with a particular significant overexpression of hsa-miR-29a-3p implicated in insulin production and secretion. Our findings suggest that <i>SLC2A2</i> mutations cause dysglycemia in FBS either by a direct effect on GLUT2 expression and/or activity or, indirectly, by the dysregulated expression of miRNAs implicated in glucose homeostasis.</p><h2>Other Information</h2><p dir="ltr">Published in: Biomedicines<br>License: <a href="https://creativecommons.org/licenses/by/4.0/" target="_blank">https://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.3390/biomedicines10092114" target="_blank">https://dx.doi.org/10.3390/biomedicines10092114</a></p>2022-08-29T09:00:00ZTextJournal contributioninfo:eu-repo/semantics/publishedVersiontextcontribution to journal10.3390/biomedicines10092114https://figshare.com/articles/journal_contribution/Understanding_the_Role_of_GLUT2_in_Dysglycemia_Associated_with_Fanconi_Bickel_Syndrome/26869528CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/268695282022-08-29T09:00:00Z
spellingShingle Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
Sanaa Sharari (12561952)
Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Medical biochemistry and metabolomics
Fanconi–Bickel syndrome (FBS)
dysglycemia
glucose transporter 2 (GLUT2)
PBMCs (peripheral blood mononuclear cells)
miRNAs
status_str publishedVersion
title Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
title_full Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
title_fullStr Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
title_full_unstemmed Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
title_short Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
title_sort Understanding the Role of GLUT2 in Dysglycemia Associated with Fanconi–Bickel Syndrome
topic Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Medical biochemistry and metabolomics
Fanconi–Bickel syndrome (FBS)
dysglycemia
glucose transporter 2 (GLUT2)
PBMCs (peripheral blood mononuclear cells)
miRNAs