Real-world experience with gene therapy in Duchenne muscular dystrophy center readiness and patients safety: report from Qatar
<p dir="ltr">Duchenne Muscular Dystrophy is a rare, X-linked neuromuscular disorder that leads to progressive muscle degeneration, loss of ambulation, and premature mortality due to respiratory and cardiac failure. Historically, Duchennke Muscular Dystrophy has been managed through s...
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2025
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