Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era

<div><p>Type 1 diabetes affects millions of people globally and requires careful management to avoid serious long-term complications, including heart and kidney disease, stroke, and loss of sight. The type 1 diabetes patient cohort is highly heterogeneous, with individuals presenting wit...

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محفوظ في:
التفاصيل البيبلوغرافية
المؤلف الرئيسي: Ammira Al-Shabeeb Akil (15143925) (author)
مؤلفون آخرون: Esraa Yassin (11618606) (author), Aljazi Al-Maraghi (14056975) (author), Elbay Aliyev (14056972) (author), Khulod Al-Malki (18324930) (author), Khalid A. Fakhro (3158862) (author)
منشور في: 2021
الموضوعات:
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author Ammira Al-Shabeeb Akil (15143925)
author2 Esraa Yassin (11618606)
Aljazi Al-Maraghi (14056975)
Elbay Aliyev (14056972)
Khulod Al-Malki (18324930)
Khalid A. Fakhro (3158862)
author2_role author
author
author
author
author
author_facet Ammira Al-Shabeeb Akil (15143925)
Esraa Yassin (11618606)
Aljazi Al-Maraghi (14056975)
Elbay Aliyev (14056972)
Khulod Al-Malki (18324930)
Khalid A. Fakhro (3158862)
author_role author
dc.creator.none.fl_str_mv Ammira Al-Shabeeb Akil (15143925)
Esraa Yassin (11618606)
Aljazi Al-Maraghi (14056975)
Elbay Aliyev (14056972)
Khulod Al-Malki (18324930)
Khalid A. Fakhro (3158862)
dc.date.none.fl_str_mv 2021-04-01T00:00:00Z
dc.identifier.none.fl_str_mv 10.1186/s12967-021-02778-6
dc.relation.none.fl_str_mv https://figshare.com/articles/journal_contribution/Diagnosis_and_treatment_of_type_1_diabetes_at_the_dawn_of_the_personalized_medicine_era/25764333
dc.rights.none.fl_str_mv CC BY 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biomedical and clinical sciences
Clinical sciences
Type 1 diabetes
Autoimmunity
Personalized medicine
Personalized treatment
Genomic Risk Score
Insulin therapy
Stem cells
Gene polymorphism
Gene therapy
Pancreatic β cells
dc.title.none.fl_str_mv Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
dc.type.none.fl_str_mv Text
Journal contribution
info:eu-repo/semantics/publishedVersion
text
contribution to journal
description <div><p>Type 1 diabetes affects millions of people globally and requires careful management to avoid serious long-term complications, including heart and kidney disease, stroke, and loss of sight. The type 1 diabetes patient cohort is highly heterogeneous, with individuals presenting with disease at different stages and severities, arising from distinct etiologies, and overlaying varied genetic backgrounds. At present, the “one-size-fits-all” treatment for type 1 diabetes is exogenic insulin substitution therapy, but this approach fails to achieve optimal blood glucose control in many individuals. With advances in our understanding of early-stage diabetes development, diabetes stratification, and the role of genetics, type 1 diabetes is a promising candidate for a personalized medicine approach, which aims to apply “the right therapy at the right time, to the right patient”. In the case of type 1 diabetes, great efforts are now being focused on risk stratification for diabetes development to enable pre-clinical detection, and the application of treatments such as gene therapy, to prevent pancreatic destruction in a sub-set of patients. Alongside this, breakthroughs in stem cell therapies hold great promise for the regeneration of pancreatic tissues in some individuals. Here we review the recent initiatives in the field of personalized medicine for type 1 diabetes, including the latest discoveries in stem cell and gene therapy for the disease, and current obstacles that must be overcome before the dream of personalized medicine for all type 1 diabetes patients can be realized.</p><p> </p></div><h2>Other Information</h2> <p> Published in: Journal of Translational Medicine<br> License: <a href="https://creativecommons.org/licenses/by/4.0" target="_blank">https://creativecommons.org/licenses/by/4.0</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1186/s12967-021-02778-6" target="_blank">https://dx.doi.org/10.1186/s12967-021-02778-6</a></p>
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identifier_str_mv 10.1186/s12967-021-02778-6
network_acronym_str Manara2
network_name_str Manara2
oai_identifier_str oai:figshare.com:article/25764333
publishDate 2021
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spelling Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine eraAmmira Al-Shabeeb Akil (15143925)Esraa Yassin (11618606)Aljazi Al-Maraghi (14056975)Elbay Aliyev (14056972)Khulod Al-Malki (18324930)Khalid A. Fakhro (3158862)Biomedical and clinical sciencesClinical sciencesType 1 diabetesAutoimmunityPersonalized medicinePersonalized treatmentGenomic Risk ScoreInsulin therapyStem cellsGene polymorphismGene therapyPancreatic β cells<div><p>Type 1 diabetes affects millions of people globally and requires careful management to avoid serious long-term complications, including heart and kidney disease, stroke, and loss of sight. The type 1 diabetes patient cohort is highly heterogeneous, with individuals presenting with disease at different stages and severities, arising from distinct etiologies, and overlaying varied genetic backgrounds. At present, the “one-size-fits-all” treatment for type 1 diabetes is exogenic insulin substitution therapy, but this approach fails to achieve optimal blood glucose control in many individuals. With advances in our understanding of early-stage diabetes development, diabetes stratification, and the role of genetics, type 1 diabetes is a promising candidate for a personalized medicine approach, which aims to apply “the right therapy at the right time, to the right patient”. In the case of type 1 diabetes, great efforts are now being focused on risk stratification for diabetes development to enable pre-clinical detection, and the application of treatments such as gene therapy, to prevent pancreatic destruction in a sub-set of patients. Alongside this, breakthroughs in stem cell therapies hold great promise for the regeneration of pancreatic tissues in some individuals. Here we review the recent initiatives in the field of personalized medicine for type 1 diabetes, including the latest discoveries in stem cell and gene therapy for the disease, and current obstacles that must be overcome before the dream of personalized medicine for all type 1 diabetes patients can be realized.</p><p> </p></div><h2>Other Information</h2> <p> Published in: Journal of Translational Medicine<br> License: <a href="https://creativecommons.org/licenses/by/4.0" target="_blank">https://creativecommons.org/licenses/by/4.0</a><br>See article on publisher's website: <a href="https://dx.doi.org/10.1186/s12967-021-02778-6" target="_blank">https://dx.doi.org/10.1186/s12967-021-02778-6</a></p>2021-04-01T00:00:00ZTextJournal contributioninfo:eu-repo/semantics/publishedVersiontextcontribution to journal10.1186/s12967-021-02778-6https://figshare.com/articles/journal_contribution/Diagnosis_and_treatment_of_type_1_diabetes_at_the_dawn_of_the_personalized_medicine_era/25764333CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/257643332021-04-01T00:00:00Z
spellingShingle Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
Ammira Al-Shabeeb Akil (15143925)
Biomedical and clinical sciences
Clinical sciences
Type 1 diabetes
Autoimmunity
Personalized medicine
Personalized treatment
Genomic Risk Score
Insulin therapy
Stem cells
Gene polymorphism
Gene therapy
Pancreatic β cells
status_str publishedVersion
title Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
title_full Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
title_fullStr Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
title_full_unstemmed Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
title_short Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
title_sort Diagnosis and treatment of type 1 diabetes at the dawn of the personalized medicine era
topic Biomedical and clinical sciences
Clinical sciences
Type 1 diabetes
Autoimmunity
Personalized medicine
Personalized treatment
Genomic Risk Score
Insulin therapy
Stem cells
Gene polymorphism
Gene therapy
Pancreatic β cells