Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling

<p dir="ltr">Familial Mediterranean fever (FMF) is the most common auto-inflammatory disease. It is transmitted as autosomal recessive trait with mutations in MEditerranean FeVer (<i>MEFV)</i> gene. Despite a typical clinical expression, many patients have either a single...

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محفوظ في:
التفاصيل البيبلوغرافية
المؤلف الرئيسي: Meenakshi Umar (492911) (author)
مؤلفون آخرون: Andre Megarbane (3485465) (author), Jingxuan Shan (4711089) (author), Najeeb Syed (12561967) (author), Eliane Chouery (558481) (author), Elbay Aliyev (14056972) (author), Puthen Jithesh (6561377) (author), Ramzi Temanni (671528) (author), Issam Mansour (14779396) (author), Lotfi Chouchane (61840) (author), Aouatef Ismail Chouchane (14779399) (author)
منشور في: 2020
الموضوعات:
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_version_ 1864513555823329280
author Meenakshi Umar (492911)
author2 Andre Megarbane (3485465)
Jingxuan Shan (4711089)
Najeeb Syed (12561967)
Eliane Chouery (558481)
Elbay Aliyev (14056972)
Puthen Jithesh (6561377)
Ramzi Temanni (671528)
Issam Mansour (14779396)
Lotfi Chouchane (61840)
Aouatef Ismail Chouchane (14779399)
author2_role author
author
author
author
author
author
author
author
author
author
author_facet Meenakshi Umar (492911)
Andre Megarbane (3485465)
Jingxuan Shan (4711089)
Najeeb Syed (12561967)
Eliane Chouery (558481)
Elbay Aliyev (14056972)
Puthen Jithesh (6561377)
Ramzi Temanni (671528)
Issam Mansour (14779396)
Lotfi Chouchane (61840)
Aouatef Ismail Chouchane (14779399)
author_role author
dc.creator.none.fl_str_mv Meenakshi Umar (492911)
Andre Megarbane (3485465)
Jingxuan Shan (4711089)
Najeeb Syed (12561967)
Eliane Chouery (558481)
Elbay Aliyev (14056972)
Puthen Jithesh (6561377)
Ramzi Temanni (671528)
Issam Mansour (14779396)
Lotfi Chouchane (61840)
Aouatef Ismail Chouchane (14779399)
dc.date.none.fl_str_mv 2020-08-27T06:00:00Z
dc.identifier.none.fl_str_mv 10.1111/jcmm.15701
dc.relation.none.fl_str_mv https://figshare.com/articles/journal_contribution/Genome_sequencing_unveils_mutational_landscape_of_the_familial_Mediterranean_fever_Potential_implications_of_IL33_ST2_signalling/22258543
dc.rights.none.fl_str_mv CC BY 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Familial Mediterranean Fever
IL1RL1
MEFV
Whole Genome Sequencing
dc.title.none.fl_str_mv Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
dc.type.none.fl_str_mv Text
Journal contribution
info:eu-repo/semantics/publishedVersion
text
contribution to journal
description <p dir="ltr">Familial Mediterranean fever (FMF) is the most common auto-inflammatory disease. It is transmitted as autosomal recessive trait with mutations in MEditerranean FeVer (<i>MEFV)</i> gene. Despite a typical clinical expression, many patients have either a single or no mutation in <i>MEFV</i>. The current work is aimed to revisit the genetic landscape of FMF disease using high-coverage whole genome sequencing. In atypical patients (carrying a single or no mutation in <i>MEFV</i>), we revealed many rare variants in genes associated with auto-inflammatory disorders, and more interestingly, we discovered a novel variant ( a 2.1-Kb deletion) in exon 11 of <i>IL1RL1</i> gene, present only in patients. To validate and screen this patient-specific variant, a tandem of allele-specific PCR and quantitative real-time PCR was performed in 184 FMF patients and 218 healthy controls and we demonstrated that the novel deletion was absent in controls and was present in more than 19% of patients. This study sheds more light on the mutational landscape of FMF. Our discovery of a disease-specific variant in <i>IL1RL1</i> gene may constitute a novel genetic marker for FMF. This finding suggesting a potential role of the IL33/ST2 signalling in the disease pathogenicity highlights a new paradigm in FMF pathophysiology.</p><h2>Other Information</h2><p dir="ltr">Published in: Journal of Cellular and Molecular Medicine<br>License: <a href="http://creativecommons.org/licenses/by/4.0/" target="_blank">http://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="http://dx.doi.org/10.1111/jcmm.15701" target="_blank">http://dx.doi.org/10.1111/jcmm.15701</a></p>
eu_rights_str_mv openAccess
id Manara2_ed7a27bfddff580f29a824f96e795729
identifier_str_mv 10.1111/jcmm.15701
network_acronym_str Manara2
network_name_str Manara2
oai_identifier_str oai:figshare.com:article/22258543
publishDate 2020
repository.mail.fl_str_mv
repository.name.fl_str_mv
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rights_invalid_str_mv CC BY 4.0
spelling Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signallingMeenakshi Umar (492911)Andre Megarbane (3485465)Jingxuan Shan (4711089)Najeeb Syed (12561967)Eliane Chouery (558481)Elbay Aliyev (14056972)Puthen Jithesh (6561377)Ramzi Temanni (671528)Issam Mansour (14779396)Lotfi Chouchane (61840)Aouatef Ismail Chouchane (14779399)Biological sciencesGeneticsBiomedical and clinical sciencesClinical sciencesFamilial Mediterranean FeverIL1RL1MEFVWhole Genome Sequencing<p dir="ltr">Familial Mediterranean fever (FMF) is the most common auto-inflammatory disease. It is transmitted as autosomal recessive trait with mutations in MEditerranean FeVer (<i>MEFV)</i> gene. Despite a typical clinical expression, many patients have either a single or no mutation in <i>MEFV</i>. The current work is aimed to revisit the genetic landscape of FMF disease using high-coverage whole genome sequencing. In atypical patients (carrying a single or no mutation in <i>MEFV</i>), we revealed many rare variants in genes associated with auto-inflammatory disorders, and more interestingly, we discovered a novel variant ( a 2.1-Kb deletion) in exon 11 of <i>IL1RL1</i> gene, present only in patients. To validate and screen this patient-specific variant, a tandem of allele-specific PCR and quantitative real-time PCR was performed in 184 FMF patients and 218 healthy controls and we demonstrated that the novel deletion was absent in controls and was present in more than 19% of patients. This study sheds more light on the mutational landscape of FMF. Our discovery of a disease-specific variant in <i>IL1RL1</i> gene may constitute a novel genetic marker for FMF. This finding suggesting a potential role of the IL33/ST2 signalling in the disease pathogenicity highlights a new paradigm in FMF pathophysiology.</p><h2>Other Information</h2><p dir="ltr">Published in: Journal of Cellular and Molecular Medicine<br>License: <a href="http://creativecommons.org/licenses/by/4.0/" target="_blank">http://creativecommons.org/licenses/by/4.0/</a><br>See article on publisher's website: <a href="http://dx.doi.org/10.1111/jcmm.15701" target="_blank">http://dx.doi.org/10.1111/jcmm.15701</a></p>2020-08-27T06:00:00ZTextJournal contributioninfo:eu-repo/semantics/publishedVersiontextcontribution to journal10.1111/jcmm.15701https://figshare.com/articles/journal_contribution/Genome_sequencing_unveils_mutational_landscape_of_the_familial_Mediterranean_fever_Potential_implications_of_IL33_ST2_signalling/22258543CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/222585432020-08-27T06:00:00Z
spellingShingle Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
Meenakshi Umar (492911)
Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Familial Mediterranean Fever
IL1RL1
MEFV
Whole Genome Sequencing
status_str publishedVersion
title Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
title_full Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
title_fullStr Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
title_full_unstemmed Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
title_short Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
title_sort Genome sequencing unveils mutational landscape of the familial Mediterranean fever: Potential implications of IL33/ST2 signalling
topic Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Familial Mediterranean Fever
IL1RL1
MEFV
Whole Genome Sequencing