An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar

<h3>Purpose of Review</h3> <p>Cystic fibrosis (CF) is a monogenic recessive disease with multisystem involvement. The cause is a mutation in the gene that encodes the cystic fibrosis transmembrane conductance regulator (CFTR) protein. The aim is to review the literature involving t...

وصف كامل

محفوظ في:
التفاصيل البيبلوغرافية
المؤلف الرئيسي: Samer Hammoudeh (3095097) (author)
مؤلفون آخرون: Wessam Gadelhak (14070756) (author), Atqah AbdulWahab (14070759) (author), Mona Al-Langawi (14070762) (author), Ibrahim A. Janahi (14070765) (author)
منشور في: 2019
الموضوعات:
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author Samer Hammoudeh (3095097)
author2 Wessam Gadelhak (14070756)
Atqah AbdulWahab (14070759)
Mona Al-Langawi (14070762)
Ibrahim A. Janahi (14070765)
author2_role author
author
author
author
author_facet Samer Hammoudeh (3095097)
Wessam Gadelhak (14070756)
Atqah AbdulWahab (14070759)
Mona Al-Langawi (14070762)
Ibrahim A. Janahi (14070765)
author_role author
dc.creator.none.fl_str_mv Samer Hammoudeh (3095097)
Wessam Gadelhak (14070756)
Atqah AbdulWahab (14070759)
Mona Al-Langawi (14070762)
Ibrahim A. Janahi (14070765)
dc.date.none.fl_str_mv 2019-11-22T06:00:00Z
dc.identifier.none.fl_str_mv 10.1007/s40142-019-00174-7
dc.relation.none.fl_str_mv https://figshare.com/articles/journal_contribution/An_Overview_of_the_Homozygous_Cystic_Fibrosis_Transmembrane_Conductance_Regulator_Mutation_c_3700_A_G_p_Ile1234Val_in_Qatar/21597789
dc.rights.none.fl_str_mv CC BY 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Cystic fibrosis
CFTR
CFTR mutation
CFTR I1234V
dc.title.none.fl_str_mv An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
dc.type.none.fl_str_mv Text
Journal contribution
info:eu-repo/semantics/publishedVersion
text
contribution to journal
description <h3>Purpose of Review</h3> <p>Cystic fibrosis (CF) is a monogenic recessive disease with multisystem involvement. The cause is a mutation in the gene that encodes the cystic fibrosis transmembrane conductance regulator (CFTR) protein. The aim is to review the literature involving the CFTR I1234V mutation and to provide recommendations for future research activities.</p> <h3>Recent Findings</h3> <p>The prevalence rates of CFTR mutations vary across the globe. The CFTR I1234V mutation is the most common mutation in Qatar, and one of the most common in the Arabian Gulf region.</p> <h3>Summary</h3> <p>Areas for future research include testing of the CFTR transcript and activity levels in different samples including nasal cells and organoids. Another area is applying Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) technology as a tool for gene editing.</p> <h2>Other Information</h2> <p>Published in: Current Genetic Medicine Reports<br> License: <a href="https://creativecommons.org/licenses/by/4.0" target="_blank">https://creativecommons.org/licenses/by/4.0</a><br> See article on publisher's website: <a href="http://dx.doi.org/10.1007/s40142-019-00174-7" target="_blank">http://dx.doi.org/10.1007/s40142-019-00174-7</a></p>
eu_rights_str_mv openAccess
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identifier_str_mv 10.1007/s40142-019-00174-7
network_acronym_str Manara2
network_name_str Manara2
oai_identifier_str oai:figshare.com:article/21597789
publishDate 2019
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rights_invalid_str_mv CC BY 4.0
spelling An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in QatarSamer Hammoudeh (3095097)Wessam Gadelhak (14070756)Atqah AbdulWahab (14070759)Mona Al-Langawi (14070762)Ibrahim A. Janahi (14070765)Biological sciencesGeneticsBiomedical and clinical sciencesClinical sciencesCystic fibrosisCFTRCFTR mutationCFTR I1234V<h3>Purpose of Review</h3> <p>Cystic fibrosis (CF) is a monogenic recessive disease with multisystem involvement. The cause is a mutation in the gene that encodes the cystic fibrosis transmembrane conductance regulator (CFTR) protein. The aim is to review the literature involving the CFTR I1234V mutation and to provide recommendations for future research activities.</p> <h3>Recent Findings</h3> <p>The prevalence rates of CFTR mutations vary across the globe. The CFTR I1234V mutation is the most common mutation in Qatar, and one of the most common in the Arabian Gulf region.</p> <h3>Summary</h3> <p>Areas for future research include testing of the CFTR transcript and activity levels in different samples including nasal cells and organoids. Another area is applying Clustered Regularly Interspaced Short Palindromic Repeats (CRISPR) technology as a tool for gene editing.</p> <h2>Other Information</h2> <p>Published in: Current Genetic Medicine Reports<br> License: <a href="https://creativecommons.org/licenses/by/4.0" target="_blank">https://creativecommons.org/licenses/by/4.0</a><br> See article on publisher's website: <a href="http://dx.doi.org/10.1007/s40142-019-00174-7" target="_blank">http://dx.doi.org/10.1007/s40142-019-00174-7</a></p>2019-11-22T06:00:00ZTextJournal contributioninfo:eu-repo/semantics/publishedVersiontextcontribution to journal10.1007/s40142-019-00174-7https://figshare.com/articles/journal_contribution/An_Overview_of_the_Homozygous_Cystic_Fibrosis_Transmembrane_Conductance_Regulator_Mutation_c_3700_A_G_p_Ile1234Val_in_Qatar/21597789CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/215977892019-11-22T06:00:00Z
spellingShingle An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
Samer Hammoudeh (3095097)
Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Cystic fibrosis
CFTR
CFTR mutation
CFTR I1234V
status_str publishedVersion
title An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
title_full An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
title_fullStr An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
title_full_unstemmed An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
title_short An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
title_sort An Overview of the Homozygous Cystic Fibrosis Transmembrane Conductance Regulator Mutation c.3700 A>G (p.Ile1234Val) in Qatar
topic Biological sciences
Genetics
Biomedical and clinical sciences
Clinical sciences
Cystic fibrosis
CFTR
CFTR mutation
CFTR I1234V