Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years.
<p>Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years.</p>
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2025
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| _version_ | 1852018928880975872 |
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| author | Francesco Muntoni (228210) |
| author2 | James Signorovitch (672562) Nathalie Goemans (503769) Adnan Y. Manzur (7340012) Nicolae Done (10751202) Gautam Sajeev (6810248) Jiayang Li (449346) Hanane Akbarnejad (21615534) Aarushi Sharma (5216615) Susan J. Ward (3018144) Erik H. Niks (674893) Laurant Servais (21615537) Eugenio Mercuri (289290) Michela Guglieri (489528) Volker Straub (251869) Imelda de Groot (4399726) Deborah Ridout (9096296) Craig McDonald (2615428) |
| author2_role | author author author author author author author author author author author author author author author author author |
| author_facet | Francesco Muntoni (228210) James Signorovitch (672562) Nathalie Goemans (503769) Adnan Y. Manzur (7340012) Nicolae Done (10751202) Gautam Sajeev (6810248) Jiayang Li (449346) Hanane Akbarnejad (21615534) Aarushi Sharma (5216615) Susan J. Ward (3018144) Erik H. Niks (674893) Laurant Servais (21615537) Eugenio Mercuri (289290) Michela Guglieri (489528) Volker Straub (251869) Imelda de Groot (4399726) Deborah Ridout (9096296) Craig McDonald (2615428) |
| author_role | author |
| dc.creator.none.fl_str_mv | Francesco Muntoni (228210) James Signorovitch (672562) Nathalie Goemans (503769) Adnan Y. Manzur (7340012) Nicolae Done (10751202) Gautam Sajeev (6810248) Jiayang Li (449346) Hanane Akbarnejad (21615534) Aarushi Sharma (5216615) Susan J. Ward (3018144) Erik H. Niks (674893) Laurant Servais (21615537) Eugenio Mercuri (289290) Michela Guglieri (489528) Volker Straub (251869) Imelda de Groot (4399726) Deborah Ridout (9096296) Craig McDonald (2615428) |
| dc.date.none.fl_str_mv | 2025-06-27T17:40:29Z |
| dc.identifier.none.fl_str_mv | 10.1371/journal.pone.0325736.s009 |
| dc.relation.none.fl_str_mv | https://figshare.com/articles/figure/Predicted_Change_in_Imputed_and_Unimputed_NSAA_Total_Score_Up_to_60_Months_Post-Baseline_Baseline_among_Patients_with_Baseline_Age_10_Years_/29427473 |
| dc.rights.none.fl_str_mv | CC BY 4.0 info:eu-repo/semantics/openAccess |
| dc.subject.none.fl_str_mv | Medicine Genetics Environmental Sciences not elsewhere classified Biological Sciences not elsewhere classified Mathematical Sciences not elsewhere classified Chemical Sciences not elsewhere classified duchenne muscular dystrophy designing randomized trials 69 %) relative (> 18 months body mass index nsaa total score ambulatory motor function quartile range 1 dmd aged 4 div >< p daily corticosteroid regimens 5 nsaa units 6 years ). index year dmd ). initially ambulatory 6 years 5 years 16 years uz leuven steroid type run velocity receiving prednisone receiving corticosteroids prediction errors novel therapies modifying therapies meter walk mean age longitudinal data genotype class floor velocity drug development dmd </ discuss applications data source cureduchenne ), controlled studies contextualizing outcomes among n ambulatory patients 31 %). |
| dc.title.none.fl_str_mv | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. |
| dc.type.none.fl_str_mv | Image Figure info:eu-repo/semantics/publishedVersion image |
| description | <p>Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years.</p> |
| eu_rights_str_mv | openAccess |
| id | Manara_a413adbbb6ee7c9c752523dd3c2d112e |
| identifier_str_mv | 10.1371/journal.pone.0325736.s009 |
| network_acronym_str | Manara |
| network_name_str | ManaraRepo |
| oai_identifier_str | oai:figshare.com:article/29427473 |
| publishDate | 2025 |
| repository.mail.fl_str_mv | |
| repository.name.fl_str_mv | |
| repository_id_str | |
| rights_invalid_str_mv | CC BY 4.0 |
| spelling | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years.Francesco Muntoni (228210)James Signorovitch (672562)Nathalie Goemans (503769)Adnan Y. Manzur (7340012)Nicolae Done (10751202)Gautam Sajeev (6810248)Jiayang Li (449346)Hanane Akbarnejad (21615534)Aarushi Sharma (5216615)Susan J. Ward (3018144)Erik H. Niks (674893)Laurant Servais (21615537)Eugenio Mercuri (289290)Michela Guglieri (489528)Volker Straub (251869)Imelda de Groot (4399726)Deborah Ridout (9096296)Craig McDonald (2615428)MedicineGeneticsEnvironmental Sciences not elsewhere classifiedBiological Sciences not elsewhere classifiedMathematical Sciences not elsewhere classifiedChemical Sciences not elsewhere classifiedduchenne muscular dystrophydesigning randomized trials69 %) relative(> 18 monthsbody mass indexnsaa total scoreambulatory motor functionquartile range 1dmd aged 4div >< pdaily corticosteroid regimens5 nsaa units6 years ).index yeardmd ).initially ambulatory6 years5 years16 yearsuz leuvensteroid typerun velocityreceiving prednisonereceiving corticosteroidsprediction errorsnovel therapiesmodifying therapiesmeter walkmean agelongitudinal datagenotype classfloor velocitydrug developmentdmd </discuss applicationsdata sourcecureduchenne ),controlled studiescontextualizing outcomesamong nambulatory patients31 %).<p>Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years.</p>2025-06-27T17:40:29ZImageFigureinfo:eu-repo/semantics/publishedVersionimage10.1371/journal.pone.0325736.s009https://figshare.com/articles/figure/Predicted_Change_in_Imputed_and_Unimputed_NSAA_Total_Score_Up_to_60_Months_Post-Baseline_Baseline_among_Patients_with_Baseline_Age_10_Years_/29427473CC BY 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/294274732025-06-27T17:40:29Z |
| spellingShingle | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. Francesco Muntoni (228210) Medicine Genetics Environmental Sciences not elsewhere classified Biological Sciences not elsewhere classified Mathematical Sciences not elsewhere classified Chemical Sciences not elsewhere classified duchenne muscular dystrophy designing randomized trials 69 %) relative (> 18 months body mass index nsaa total score ambulatory motor function quartile range 1 dmd aged 4 div >< p daily corticosteroid regimens 5 nsaa units 6 years ). index year dmd ). initially ambulatory 6 years 5 years 16 years uz leuven steroid type run velocity receiving prednisone receiving corticosteroids prediction errors novel therapies modifying therapies meter walk mean age longitudinal data genotype class floor velocity drug development dmd </ discuss applications data source cureduchenne ), controlled studies contextualizing outcomes among n ambulatory patients 31 %). |
| status_str | publishedVersion |
| title | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. |
| title_full | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. |
| title_fullStr | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. |
| title_full_unstemmed | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. |
| title_short | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. |
| title_sort | Predicted Change in Imputed and Unimputed NSAA Total Score Up to 60 Months Post-Baseline Baseline among Patients with Baseline Age < 10 Years. |
| topic | Medicine Genetics Environmental Sciences not elsewhere classified Biological Sciences not elsewhere classified Mathematical Sciences not elsewhere classified Chemical Sciences not elsewhere classified duchenne muscular dystrophy designing randomized trials 69 %) relative (> 18 months body mass index nsaa total score ambulatory motor function quartile range 1 dmd aged 4 div >< p daily corticosteroid regimens 5 nsaa units 6 years ). index year dmd ). initially ambulatory 6 years 5 years 16 years uz leuven steroid type run velocity receiving prednisone receiving corticosteroids prediction errors novel therapies modifying therapies meter walk mean age longitudinal data genotype class floor velocity drug development dmd </ discuss applications data source cureduchenne ), controlled studies contextualizing outcomes among n ambulatory patients 31 %). |