Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule

1,25-Dihydroxyvitamin D (1,25D) analogs engage the vitamin D receptor (VDR) and can exert anticancer and immunomodulatory effects. Although tumors often resist 1,25D monotherapy, combining VDR agonism with histone deacetylase inhibitors (HDACi) restores anticancer efficacy. Here, we present AC-340,...

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محفوظ في:
التفاصيل البيبلوغرافية
المؤلف الرئيسي: Fatemeh Sarmadi (18865539) (author)
مؤلفون آخرون: Amelia Caza (22273467) (author), Zhizhong Gao (18865542) (author), Natacha Rochel (225991) (author), James L. Gleason (1853971) (author), John H. White (63329) (author)
منشور في: 2025
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author Fatemeh Sarmadi (18865539)
author2 Amelia Caza (22273467)
Zhizhong Gao (18865542)
Natacha Rochel (225991)
James L. Gleason (1853971)
John H. White (63329)
author2_role author
author
author
author
author
author_facet Fatemeh Sarmadi (18865539)
Amelia Caza (22273467)
Zhizhong Gao (18865542)
Natacha Rochel (225991)
James L. Gleason (1853971)
John H. White (63329)
author_role author
dc.creator.none.fl_str_mv Fatemeh Sarmadi (18865539)
Amelia Caza (22273467)
Zhizhong Gao (18865542)
Natacha Rochel (225991)
James L. Gleason (1853971)
John H. White (63329)
dc.date.none.fl_str_mv 2025-09-19T02:55:31Z
dc.identifier.none.fl_str_mv 10.1021/acs.jmedchem.5c01932.s002
dc.relation.none.fl_str_mv https://figshare.com/articles/dataset/Hyperagonism_of_a_Vitamin_D_Receptor_Agonist_Histone_Deacetylase_Inhibitor_Hybrid_Molecule/30162201
dc.rights.none.fl_str_mv CC BY-NC 4.0
info:eu-repo/semantics/openAccess
dc.subject.none.fl_str_mv Biophysics
Biochemistry
Medicine
Cell Biology
Genetics
Molecular Biology
Pharmacology
Developmental Biology
Cancer
Virology
Biological Sciences not elsewhere classified
Chemical Sciences not elsewhere classified
novel bifunctional molecule
multiple melanoma models
multiple cancer models
histone deacetylase inhibitors
elevated h3k27 acetylation
comparative structural studies
restores anticancer efficacy
vdr target genes
combining vdr agonism
vdr agonist backbone
340 hdaci activity
exert anticancer
vdr hyperagonist
robust bifunctionality
rnaseq analysis
receptor agonist
qpcr revealed
likely coupled
incorporates hdaci
immunomodulatory effects
combination therapies
coactivator cbp
broad array
analogs engage
active transcription
340 superinduces
340 functions
340 forms
dc.title.none.fl_str_mv Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
dc.type.none.fl_str_mv Dataset
info:eu-repo/semantics/publishedVersion
dataset
description 1,25-Dihydroxyvitamin D (1,25D) analogs engage the vitamin D receptor (VDR) and can exert anticancer and immunomodulatory effects. Although tumors often resist 1,25D monotherapy, combining VDR agonism with histone deacetylase inhibitors (HDACi) restores anticancer efficacy. Here, we present AC-340, a novel bifunctional molecule that incorporates HDACi into a VDR agonist backbone. Besides its robust bifunctionality in vitro in multiple melanoma models, RNaseq analysis of B16–F10 mouse melanoma cells revealed that AC-340 superinduces the expression of a broad array of VDR target genes. Comparative structural studies and ChIP-qPCR revealed that AC-340 forms more interactions than 1,25D with residues in the VDR coactivator binding domain, leading to more efficacious recruitment of coactivator CBP. This, likely coupled with AC-340 HDACi activity, leads to elevated H3K27 acetylation of VDR target genes, a mark of active transcription. Thus, AC-340 functions as a VDR hyperagonist and should be efficacious in mono- or combination therapies against multiple cancer models.
eu_rights_str_mv openAccess
id Manara_b01bb7d64aab28a5f716ffecd41dc34d
identifier_str_mv 10.1021/acs.jmedchem.5c01932.s002
network_acronym_str Manara
network_name_str ManaraRepo
oai_identifier_str oai:figshare.com:article/30162201
publishDate 2025
repository.mail.fl_str_mv
repository.name.fl_str_mv
repository_id_str
rights_invalid_str_mv CC BY-NC 4.0
spelling Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid MoleculeFatemeh Sarmadi (18865539)Amelia Caza (22273467)Zhizhong Gao (18865542)Natacha Rochel (225991)James L. Gleason (1853971)John H. White (63329)BiophysicsBiochemistryMedicineCell BiologyGeneticsMolecular BiologyPharmacologyDevelopmental BiologyCancerVirologyBiological Sciences not elsewhere classifiedChemical Sciences not elsewhere classifiednovel bifunctional moleculemultiple melanoma modelsmultiple cancer modelshistone deacetylase inhibitorselevated h3k27 acetylationcomparative structural studiesrestores anticancer efficacyvdr target genescombining vdr agonismvdr agonist backbone340 hdaci activityexert anticancervdr hyperagonistrobust bifunctionalityrnaseq analysisreceptor agonistqpcr revealedlikely coupledincorporates hdaciimmunomodulatory effectscombination therapiescoactivator cbpbroad arrayanalogs engageactive transcription340 superinduces340 functions340 forms1,25-Dihydroxyvitamin D (1,25D) analogs engage the vitamin D receptor (VDR) and can exert anticancer and immunomodulatory effects. Although tumors often resist 1,25D monotherapy, combining VDR agonism with histone deacetylase inhibitors (HDACi) restores anticancer efficacy. Here, we present AC-340, a novel bifunctional molecule that incorporates HDACi into a VDR agonist backbone. Besides its robust bifunctionality in vitro in multiple melanoma models, RNaseq analysis of B16–F10 mouse melanoma cells revealed that AC-340 superinduces the expression of a broad array of VDR target genes. Comparative structural studies and ChIP-qPCR revealed that AC-340 forms more interactions than 1,25D with residues in the VDR coactivator binding domain, leading to more efficacious recruitment of coactivator CBP. This, likely coupled with AC-340 HDACi activity, leads to elevated H3K27 acetylation of VDR target genes, a mark of active transcription. Thus, AC-340 functions as a VDR hyperagonist and should be efficacious in mono- or combination therapies against multiple cancer models.2025-09-19T02:55:31ZDatasetinfo:eu-repo/semantics/publishedVersiondataset10.1021/acs.jmedchem.5c01932.s002https://figshare.com/articles/dataset/Hyperagonism_of_a_Vitamin_D_Receptor_Agonist_Histone_Deacetylase_Inhibitor_Hybrid_Molecule/30162201CC BY-NC 4.0info:eu-repo/semantics/openAccessoai:figshare.com:article/301622012025-09-19T02:55:31Z
spellingShingle Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
Fatemeh Sarmadi (18865539)
Biophysics
Biochemistry
Medicine
Cell Biology
Genetics
Molecular Biology
Pharmacology
Developmental Biology
Cancer
Virology
Biological Sciences not elsewhere classified
Chemical Sciences not elsewhere classified
novel bifunctional molecule
multiple melanoma models
multiple cancer models
histone deacetylase inhibitors
elevated h3k27 acetylation
comparative structural studies
restores anticancer efficacy
vdr target genes
combining vdr agonism
vdr agonist backbone
340 hdaci activity
exert anticancer
vdr hyperagonist
robust bifunctionality
rnaseq analysis
receptor agonist
qpcr revealed
likely coupled
incorporates hdaci
immunomodulatory effects
combination therapies
coactivator cbp
broad array
analogs engage
active transcription
340 superinduces
340 functions
340 forms
status_str publishedVersion
title Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
title_full Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
title_fullStr Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
title_full_unstemmed Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
title_short Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
title_sort Hyperagonism of a Vitamin D Receptor Agonist/Histone Deacetylase Inhibitor Hybrid Molecule
topic Biophysics
Biochemistry
Medicine
Cell Biology
Genetics
Molecular Biology
Pharmacology
Developmental Biology
Cancer
Virology
Biological Sciences not elsewhere classified
Chemical Sciences not elsewhere classified
novel bifunctional molecule
multiple melanoma models
multiple cancer models
histone deacetylase inhibitors
elevated h3k27 acetylation
comparative structural studies
restores anticancer efficacy
vdr target genes
combining vdr agonism
vdr agonist backbone
340 hdaci activity
exert anticancer
vdr hyperagonist
robust bifunctionality
rnaseq analysis
receptor agonist
qpcr revealed
likely coupled
incorporates hdaci
immunomodulatory effects
combination therapies
coactivator cbp
broad array
analogs engage
active transcription
340 superinduces
340 functions
340 forms