Different Niemann-Pick C1 Genotypes Generate Protein Phenotypes that Vary in their Intracellular Processing, Trafficking and Localization

Niemann-Pick Type C (NP-C) is an inherited neurovisceral lysosomal storage disease characterized by a defect in the trafficking of endocytosed cholesterol. In 95% of patients the gene encoding NPC1 is affected. The correlation of the genetic background in NP-C with the clinical phenotype such as, se...

Full description

Saved in:
Bibliographic Details
Main Author: Shammas, Hadeel (author)
Other Authors: Kuech, Eva-Maria (author), Rizk, Sandra (author), Das, Anibh M. (author), Naim, Hassan Y. (author)
Format: article
Published: 2019
Online Access:http://hdl.handle.net/10725/11322
https://doi.org/10.1038/s41598-019-41707-y
http://libraries.lau.edu.lb/research/laur/terms-of-use/articles.php
https://www.nature.com/articles/s41598-019-41707-y
Tags: Add Tag
No Tags, Be the first to tag this record!